C3 partners with 16 LGMD organizations in letter to FDA
Coalition to Cure Calpain 3 is proud to be one of 17 organizations dedicated to LGMD to have collaborated on a statement submitted to the Food and Drug Administration in conjunction with the recent Patient-Focused Drug Development Meeting Patient Perspectives on Gene Therapy Products.
A new paper, “CaMKIIβ Signaling drives expression of metabolic and stress response genes in skeletal muscle, and its loss contributes to the LGMDR1 phenotype,” was recently published in the journal Human Molecular Genetics. It was authored by a multi-institutional group led by Dr. Melissa Spencer, C3 Scientific Advisory Board Chair and Professor of Neurology and... Read More
C3 was proudly represented in Washington, D.C. at the 2026 LGMD Day on the Hill, hosted by The Speak Foundation. C3 Advocacy Chair Melina Garza was selected as a 2026 delegate and had the privilege of leading the Texas and North Carolina delegation through a packed day of advocacy on Capitol Hill. The day began... Read More