Sarepta Therapeutics recently joined C3 to present a community webinar titled “Journey Update for the LGMD2A/R1 Calpainopathy Community.” During the webinar, Sarepta discussed the essential role for natural history studies throughout the drug development process. They then shared the design
C3 hosts Sarepta to present webinar about the JOURNEY natural history study
Click here to register!
Trial readiness study for individuals with LGMD2A/R1
Please contact either Ruby Langeslay or Jennifer Raymond at Virginia Commonwealth University for more information
Casimir Recruiting LGMD2A/R1 Patients for At-Home Study
The Casimir LGVA study is quickly filling! We are specifically seeking individuals with LGMD2A who can walk across a room and stand up from sitting on a couch to participate. Email LGMDS@casimirtrials.com or call (800)542-0948 for more information.
Have you participated in a clinical research study?
Attention Individuals with LGMD2A/R1: Coalition to Cure Calpain 3 wants to hear from you! If you have participated in clinical research, such as a natural history study, an observational study, or a clinical trial, please follow this link to answer
Will YOU help advance LGMD2A/R1 research by participating in the GRASP-LGMD Natural History Study?
Natural history studies collect information about the symptoms and progression of a disease in the absence of an intervention. It is vital to understand natural history so that researchers can plan for clinical trials to determine if an investigational drug
LGMD2A/R1 Patient Enrollment Underway for C3-Sponsored Natural History Study
The GRASP-LGMD consortium is currently recruiting for a natural history study for individuals with mutations in CAPN3 (calpain 3). This study will inform the design of future therapeutic trials and a better understanding of the disease. Participants can now enroll at
C3 is Connecting Patients to Clinical Studies
Coalition to Cure Calpain 3 is a vital hub connecting patients with limb-girdle muscular dystrophy type 2A (LGMD2A/R1) to clinical studies. In celebration of ten years of progress in our mission to fund research for a cure and raise global awareness, we
Patient Recruitment Underway for C3-Sponsored Natural History Study
The GRASP-LGMD is currently recruiting for a natural history study for individuals with mutations in CAPN3 (calpain 3). This study will inform the design of future therapeutic trials and a better understanding of the disease. Participants can now enroll at Virginia
May 20 is Clinical Trials Day
Clinical Trials Day occurs every year on May 20 to recognize the people who conduct clinical research trials and to provide an opportunity to raise awareness of clinical trials. This date was chosen to commemorate the day that James Lind