Research Projects

Two new research projects funded to explore potential treatments for calpainopathy/LGMD2A $500,000+ committed to gene therapy research since initiative launched in 2017 Coalition to Cure Calpain 3 (C3), a non-profit patient advocacy organization focused on identifying and advancing potential treatments

FOURTH GENE THERAPY INITIATIVE GRANT SUPPORTS PROMISING RESEARCH AT NATIONWIDE CHILDREN’S HOSPITAL Coalition to Cure Calpain 3 (C3) is excited to announce that a new research grant has been awarded to Dr. Zarife Sahenk, Professor of Pediatrics and Neurology at

Coalition to Cure Calpain 3 (C3) is pleased to announce that we are funding a new research grant to Dr. Kathryn Wagner.  Dr. Wagner, Director of the Center for Genetic Muscle Disorders at the Kennedy Krieger Institute and Professor of

Coalition to Cure Calpain 3 (C3) is excited to announce that a new research grant has been awarded to Dr. Isabelle Richard, Researcher at Généthon, to analyze a novel model of calpainopathy and utilize it for the development of adeno-associated

PRIME TIME FOR GENE THERAPY While its potential has been discussed and studied for decades, 2017 was a year that showed the promise of gene therapy becoming a reality for patients. The FDA approved the first gene therapies in the

Coalition to Cure Calpain 3 (C3) is proud to support September 30 “Limb Girdle MD Awareness Day” with the announcement that we are awarding a new research grant to Dr. Michele Calos, Professor in the Department of Genetics at Stanford

Coalition to Cure Calpain 3 (C3) is excited to announce that we are funding a new research project with Dr. Rita Perlingeiro, Professor of Medicine and Lillehei Professor in Stem Cell and Regenerative Cardiovascular Medicine at the University of Minnesota.

Coalition to Cure Calpain 3 (C3) is excited to announce that we are funding a new research project with Dr. Melissa Spencer at the University of California Los Angeles. The project is titled “Identification of calpain 3 substrates through use